Large-scale expansions of Friedreich's ataxia GAA•TTC repeats in an experimental human system: role of DNA replication and prevention by LNA-DNA oligonucleotides and PNA oligomers

  1. Rastokina, A.
  2. Cebrián, J.
  3. Mozafari, N.
  4. Mandel, N.H.
  5. Smith, C.I.E.
  6. Lopes, M.
  7. Zain, R.
  8. Mirkin, S.M.
Zeitschrift:
Nucleic Acids Research

ISSN: 1362-4962 0305-1048

Datum der Publikation: 2023

Ausgabe: 51

Nummer: 16

Seiten: 8532-8549

Art: Artikel

DOI: 10.1093/NAR/GKAD441 GOOGLE SCHOLAR lock_openOpen Access editor