Effective AAV-mediated gene replacement therapy in retinal organoids modeling AIPL1-associated LCA4

  1. Sai, H.
  2. Ollington, B.
  3. Rezek, F.O.
  4. Chai, N.
  5. Lane, A.
  6. Georgiadis, T.
  7. Bainbridge, J.
  8. Michaelides, M.
  9. Sacristan-Reviriego, A.
  10. Perdigão, P.R.L.
  11. Leung, A.
  12. van der Spuy, J.
Journal:
Molecular Therapy Nucleic Acids

ISSN: 2162-2531

Year of publication: 2024

Volume: 35

Issue: 1

Type: Article

DOI: 10.1016/J.OMTN.2024.102148 GOOGLE SCHOLAR lock_openOpen access editor
Data source: Scopus