LEOPOLDO
PÉREZ DE ISLA
Profesor asociado de Ciencias de la Salud
Universidade Federal do Rio de Janeiro
Río de Janeiro, BrasilPublications en collaboration avec des chercheurs de Universidade Federal do Rio de Janeiro (1)
2021
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Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study
The Lancet Neurology, Vol. 20, Núm. 1, pp. 49-59