Publications in collaboration with researchers from University of Paris-Saclay (2)

2023

  1. Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

    Neurology and Therapy, Vol. 12, Núm. 5, pp. 1759-1775

2021

  1. Long-term safety and efficacy of patisiran for hereditary transthyretin-mediated amyloidosis with polyneuropathy: 12-month results of an open-label extension study

    The Lancet Neurology, Vol. 20, Núm. 1, pp. 49-59