Publicaciones en colaboración con investigadores/as de University College London (2)

2020

  1. Experimental gene therapies for the NCLs

    Biochimica et Biophysica Acta - Molecular Basis of Disease, Vol. 1866, Núm. 9

2019

  1. Neonatal brain-directed gene therapy rescues a mouse model of neurodegenerative CLN6 Batten disease

    Human Molecular Genetics, Vol. 28, Núm. 23, pp. 3867-3879